Akyol, M. U.,
Alden, T. D., Amartino, H., Ashworth, J., Belani, K., Berger, K. I., Borgo, A., Braunlin, E., Eto, Y., Gold, J. I., Jester, A., Jones, S. A., Karsli, C., Mackenzie, W., Marinho, D. R., McFadyen, A., McGill, J., Mitchell, J. J., Muenzer, J., Okuyama, T.,
& 9 othersOrchard, P. J., Stevens, B., Thomas, S., Walker, R., Wynn, R., Giugliani, R., Harmatz, P., Hendriksz, C. & Scarpa, M.,
Jun 13 2019,
In: Orphanet journal of rare diseases. 14,
1, 137.
Research output: Contribution to journal › Article › peer-review