Grants per year
- 1 - 25 out of 47 results
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Active
A Phase 2 Open-Label Long-Term Extension Study to Evaluate the Safety and Efficacy of BMN 111 in Children with Achondroplasia
Charrow, J. (PD/PI)
3/12/20 → 8/31/50
Project: Research project
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Natural history study for pediatric patients with early onset of either GM1 gangliosidosis, GM2 gangliosidoses, or Gaucher disease type 2
Charrow, J. (PD/PI)
11/6/19 → 8/31/50
Project: Research project
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A Phase 1/2 Study of ARQ 092 (Miransertib) in Subjects with PIK3CA-related Overgrowth Spectrum and Proteus Syndrome
Charrow, J. (PD/PI)
4/25/19 → 8/31/50
Project: Research project
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BMN 111-302: A Phase 3, Open-Label Long-Term Extension Study to Evaluate the Safety and Efficacy of BMN 111 in Children with Achondroplasia
Charrow, J. (PD/PI)
12/18/18 → 8/31/50
Project: Research project
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Protalix PB-102-F20: A Randomized, Double blind, Active Control Study of the Safety and Efficacy of PRX-102 compared to Agalsidase Beta on Renal Function in Patients with Fabry Disease Previously Treated With Agalsidase Beta
Burton, B. K. (PD/PI) & Charrow, J. (PD/PI)
5/16/18 → 8/31/50
Project: Research project
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EFC-14028: A Phase 3 Randomized, Multicenter, Multinational, Double-Blinded Study Comparing the Efficacy and Safety of Repeated Biweekly Infusions of neoGAA (GZ402666) and Alglucosidase Alfa
Burton, B. K. (PD/PI) & Charrow, J. (PD/PI)
12/11/17 → 8/31/50
Project: Research project
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BMN 111-301: A Phase 3 Randomized, Double-Blind, Placebo-Controlled, Multicenter Study to Evaluate the Efficacy and Safety of BMN 111 in Children with Achondroplasia
Charrow, J. (PD/PI) & Burton, B. K. (Co-Investigator)
10/1/17 → 8/31/50
Project: Research project
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Shire SHP-GCB-402: An Open-label, Multicenter, Single-arm, Phase 4 Study of the Effect of Treatment with Velaglucerase alfa on Bone-related Pathology in Treatment-naive Patients with Type 1 Gaucher Disease
Burton, B. K. (PD/PI) & Charrow, J. (PD/PI)
Shire Human Genetic Therapies, Inc.
6/30/17 → 8/31/50
Project: Research project
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MARS: Morquio A Registry
Burton, B. K. (PD/PI) & Charrow, J. (Co-Investigator)
12/15/14 → 8/31/50
Project: Research project
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HGT-MLD-092: Natural History Study of Children with Metachromatic Leukodystrophy
Burton, B. K. (PD/PI), Charrow, J. (PD/PI), Ida, J. B. (PD/PI) & Kuntz, N. L. (PD/PI)
Shire Human Genetic Therapies, Inc.
12/20/13 → 8/31/50
Project: Research project
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HPN-100-014: Long-Term Registry of Patients With Urea Cycle Disorders (UCDs) - THRIVE
Burton, B. K. (PD/PI) & Charrow, J. (Co-Investigator)
12/11/13 → 8/31/50
Project: Research project
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Finished
Lysosomal Storage Disease Focused Fellowship 2021
Charrow, J. (PD/PI)
8/1/20 → 7/31/21
Project: Research project
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Genetic Counseling 2021
Charrow, J. (PD/PI)
Illinois Department of Public Health
7/1/20 → 6/30/21
Project: Research project
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Lysosomal Storage Disease Training Program for Genetic Counselors
Charrow, J. (PD/PI)
9/1/18 → 7/31/21
Project: Research project
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Lysosomal Storage Disease Training Program for Genetic Counselors
Charrow, J. (PD/PI)
9/1/18 → 7/31/21
Project: Research project
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Lysosomal Storage Disease Training Program for Genetic Counselors
Charrow, J. (PD/PI)
9/1/18 → 7/31/21
Project: Research project
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A Phase 2, Open-Label, Extension Study to Evaluate the Long-Term Safety, Tolerability, and Efficacy of BMN 111 in Children with Achondroplasia
Charrow, J. (PD/PI) & Burton, B. K. (Co-Investigator)
1/21/16 → 9/30/24
Project: Research project
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AGT-182-101: A Phase 1 Safety and Dose-Finding Study of a Human Insulin Receptor Monoclonal Antibody-Human Iduronate 2-Sulfatase (IDS) Fusion Protein, AGT-182 in Adult Patients with Mucopolysaccharidosis II (MPS II, Hunter Syn
Burton, B. K. (PD/PI), Alden, T. D. (Co-Investigator), Charrow, J. (Co-Investigator) & Epstein, L. G. (Co-Investigator)
10/1/15 → 10/1/16
Project: Research project
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AGT-181-102: A Phase 1 Safety and Dose-Finding Study of a Human Insulin Receptor Monoclonal Antibody-Human alpha-L-iduronidase (HIRMAb-IDUA) Fusion Protein, AGT-181 in Adult Patients with Mucopolysaccharidosis I (MPS I)
Burton, B. K. (PD/PI), Alden, T. D. (Co-Investigator) & Charrow, J. (Co-Investigator)
9/24/15 → 12/31/16
Project: Research project
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SHP-609-302: An Open Label Extension of Study HGT-HIT-094 Evaluating Long Term Safety and Clinical Outcomes of Intrathecal Idursulfase Administered in Conjunction with Elaprase® in Patients with Hunter Syndrome and Cognitive Im
Alden, T. D. (PD/PI), Burton, B. K. (PD/PI), Charrow, J. (PD/PI) & Rinaldi, J. A. (PD/PI)
Shire Human Genetic Therapies, Inc.
6/15/15 → 12/31/19
Project: Research project
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SHP-ELA-401: A Long-Term, Open-Label, Multicenter, Phase IV Study to Assess Longitudinal Changes on Height and Weight in Patients with MPS II Who Are Receiving Elaprase and Started Treatment With Elaprase at <6 Years of Age
Burton, B. K. (PD/PI) & Charrow, J. (PD/PI)
Shire Human Genetic Therapies, Inc.
4/13/15 → 6/4/21
Project: Research project
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Lysosomal Storage Disease Training Program for Genetic Counselors
Charrow, J. (PD/PI)
4/1/15 → 3/31/16
Project: Research project
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HGT-HIT-046: An Open-Label Extension of Study HGT-HIT-045 Evaluating Long-Term Safety and Clinical Outcomes of Intrathecal Idursulfase-IT Administered inConjunction with Intravenous Elaprase® in Pediatric Patients with Hunter
Alden, T. D. (PD/PI), Burton, B. K. (PD/PI) & Charrow, J. (PD/PI)
Shire Human Genetic Therapies, Inc.
11/24/14 → 12/31/16
Project: Research project
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701-301: A Phase 3 Switchover Study of the Efficacy and Safety of BMN 701 (Gilt-tagged Recombinant Human GAA) and Long-Term Study for Extended Treatment in rhGAA Exposed Subjects with Late-onset Pompe disease.
Charrow, J. (PD/PI) & Burton, B. K. (Co-Investigator)
9/2/14 → 2/25/17
Project: Research project