Grants per year
Search results
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Active
A Phase 2 Open-Label Long-Term Extension Study to Evaluate the Safety and Efficacy of BMN 111 in Children with Achondroplasia
Charrow, J. (PD/PI)
3/12/20 → 8/31/50
Project: Research project
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Natural history study for pediatric patients with early onset of either GM1 gangliosidosis, GM2 gangliosidoses, or Gaucher disease type 2
Charrow, J. (PD/PI)
11/6/19 → 8/31/50
Project: Research project
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A Phase 1/2 Study of ARQ 092 (Miransertib) in Subjects with PIK3CA-related Overgrowth Spectrum and Proteus Syndrome
Charrow, J. (PD/PI)
4/25/19 → 8/31/50
Project: Research project
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BMN 111-302: A Phase 3, Open-Label Long-Term Extension Study to Evaluate the Safety and Efficacy of BMN 111 in Children with Achondroplasia
Charrow, J. (PD/PI)
12/18/18 → 8/31/50
Project: Research project
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Protalix PB-102-F20: A Randomized, Double blind, Active Control Study of the Safety and Efficacy of PRX-102 compared to Agalsidase Beta on Renal Function in Patients with Fabry Disease Previously Treated With Agalsidase Beta
Burton, B. K. (PD/PI) & Charrow, J. (PD/PI)
5/16/18 → 8/31/50
Project: Research project
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EFC-14028: A Phase 3 Randomized, Multicenter, Multinational, Double-Blinded Study Comparing the Efficacy and Safety of Repeated Biweekly Infusions of neoGAA (GZ402666) and Alglucosidase Alfa
Burton, B. K. (PD/PI) & Charrow, J. (PD/PI)
12/11/17 → 8/31/50
Project: Research project
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BMN 111-301: A Phase 3 Randomized, Double-Blind, Placebo-Controlled, Multicenter Study to Evaluate the Efficacy and Safety of BMN 111 in Children with Achondroplasia
Charrow, J. (PD/PI) & Burton, B. K. (Co-Investigator)
10/1/17 → 8/31/50
Project: Research project
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Shire SHP-GCB-402: An Open-label, Multicenter, Single-arm, Phase 4 Study of the Effect of Treatment with Velaglucerase alfa on Bone-related Pathology in Treatment-naive Patients with Type 1 Gaucher Disease
Burton, B. K. (PD/PI) & Charrow, J. (PD/PI)
Shire Human Genetic Therapies, Inc.
6/30/17 → 8/31/50
Project: Research project
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MARS: Morquio A Registry
Burton, B. K. (PD/PI) & Charrow, J. (Co-Investigator)
12/15/14 → 8/31/50
Project: Research project
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HGT-MLD-092: Natural History Study of Children with Metachromatic Leukodystrophy
Burton, B. K. (PD/PI), Charrow, J. (PD/PI), Ida, J. B. (PD/PI) & Kuntz, N. L. (PD/PI)
Shire Human Genetic Therapies, Inc.
12/20/13 → 8/31/50
Project: Research project
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HPN-100-014: Long-Term Registry of Patients With Urea Cycle Disorders (UCDs) - THRIVE
Burton, B. K. (PD/PI) & Charrow, J. (Co-Investigator)
12/11/13 → 8/31/50
Project: Research project