232SM201: An Open-Label Study to Assess the Efficacy, Safety, Tolerability, and Pharmacokinetics of Multiple Doses of ISIS 396443 Delivered Intrathecally to Subjects with Genetically Diagnosed and Presymptomatic Spinal Muscular

Project: Research project

Project Details

StatusFinished
Effective start/end date4/1/153/31/20

Funding

  • Biogen IDEC
  • Biogen IDEC