396443-CS4: A Phase 3, Randomized, Double-blind, Sham-Procedure Controlled Study to Assess the Clinical Efficacy and Safety of ISIS 396443 Administered Intrathecally in Patients with Later-onset Spinal Muscular Atrophy.

Project: Research project

Project Details

StatusFinished
Effective start/end date1/1/15 → 2/26/18

Funding

  • Ionis Pharmaceuticals, Inc.