A Phase 3, Randomized, Double-blind, Sham-Procedure Controlled Study to Assess the Clinical Efficacy and Safety of ISIS 396443 Administered Intrathecally in Patients with Infantile-onset Spinal Muscular Atrophy

Project: Research project

Project Details

StatusActive
Effective start/end date9/1/14 → 8/31/50

Funding

  • Ionis Pharmaceuticals, Inc.