BMN 270-301: A Phase 3 Open-Label, Single-Arm Study To Evaluate The Efficacy and Safety of BMN 270, an Adeno-Associated Virus Vector-Mediated Gene Transfer of Human Factor VIII in Hemophilia A Patients with Residual FVIII Level

Project: Research project

Project Details

StatusActive
Effective start/end date3/12/198/31/50

Funding

  • BioMarin Pharmaceutical Inc.