FIREFISH BP39056: A TWO PART SEAMLESS, OPEN-LABEL, MULTICENTER STUDY TO INVESTIGATE THE SAFETY, TOLERABILITY, PHARMACOKINETICS, PHARMACODYNAMICS AND EFFICACY OF RO7034067 IN INFANTS WITH TYPE 1 SPINAL MUSCULAR ATROPHY

Project: Research project

Project Details

StatusFinished
Effective start/end date11/8/1712/30/20

Funding

  • Roche TCRC, Inc.