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FIREFISH BP39056: A TWO PART SEAMLESS, OPEN-LABEL, MULTICENTER STUDY TO INVESTIGATE THE SAFETY, TOLERABILITY, PHARMACOKINETICS, PHARMACODYNAMICS AND EFFICACY OF RO7034067 IN INFANTS WITH TYPE 1 SPINAL MUSCULAR ATROPHY
Kuntz, Nancy L
(PD/PI)
Pediatrics
Project
:
Research project
Overview
Project Details
Status
Finished
Effective start/end date
11/8/17
→
12/30/20
Funding
Roche TCRC, Inc.
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