LALDR: An Observational Disease and Clinical Outcomes Registry of Patients with Lysosomal Acid Lipase (LAL) Deficiency (Wolman Disease and Cholesteryl Ester Storage Disease) and Carriers of the Disorder.

Project: Research project

Project Details

StatusFinished
Effective start/end date2/1/16 → 2/29/20

Funding

  • Alexion Pharmaceuticals, Inc