Prot #AVXS-101-CL-303: A Phase 3, Open-Label, Single-Arm, Single-Dose Gene Replacement Therapy Clinical Trial for Patients with Spinal Muscular Atrophy Type 1 with One or Two SMN2 Copies Delivering AVXS-101 by Intravenous Infusion (STRIVE)
- Krosschell, Kristin (PD/PI)
Project: Research project