Protocol 232SM201: An Open-Label Study to Assess the Efficacy, Safety, Tolerability, and Pharmacokinetics of Multiple Doses of ISIS 396443 Delivered Intrathecally to Subjects With Genetically Diagnosed and Presymptomatic Spinal Muscular Atropy” (Protocol

Project: Research project

Project Details

StatusActive
Effective start/end date10/22/1510/31/22

Funding

  • Ann & Robert H. Lurie Children's Hospital of Chicago (232SM201)
  • Biogen Inc. (232SM201)