Protocol No. ISIS 396443-CS4: A Phase 3, Randomized, Double-blind, Sham-Procedure Controlled Study to Assess the Clinical Efficacy and Safety of ISIS 396443 Administered Intrathecally in Patients with Later-onset Spinal Muscular Atrophy

Project: Research project

Project Details

Effective start/end date3/3/153/3/18


  • Ann & Robert H. Lurie Children's Hospital of Chicago (Protocol No. ISIS 396443-CS4)
  • Isis Pharmaceuticals, Inc. (Protocol No. ISIS 396443-CS4)