Prot#UX701-CL301: A Randomized, Double-Blind, Placebo-Controlled, Multicenter, Seamless, Adaptive, Safety, Dose-Finding, and Phase 3 Clinical Study of UX701 AAV-Mediated Gene Transfer for the Treatment of Wilson Disease

Project: Research project

Project Details

StatusActive
Effective start/end date5/27/21 → 5/31/25

Funding

  • PPD Investigator Services, LLC (Prot#UX701-CL301 Amnd 2 // Prot#UX701-CL301 Amnd 2)
  • Ultragenyx Pharmaceutical Inc. (Prot#UX701-CL301 Amnd 2 // Prot#UX701-CL301 Amnd 2)