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PTC124-GD-021e-CF: A PHASE 3 EXTENSION STUDY OF ATALUREN (PTC124) IN PATIENTS WITH NONSENSE MUTATION CYSTIC FIBROSIS
McColley, Susanna A
(PD/PI)
Pediatrics
Project
:
Research project
Overview
Project Details
Status
Finished
Effective start/end date
9/30/15
→
12/31/18
Funding
PTC Therapeutics, Inc.
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