Allele-selective transcriptional repression of mutant HTT for the treatment of Huntington’s disease

Bryan Zeitler*, Steven Froelich, Kimberly Marlen, David A. Shivak, Qi Yu, Davis Li, Jocelynn R. Pearl, Jeffrey C. Miller, Lei Zhang, David E. Paschon, Sarah J. Hinkley, Irina Ankoudinova, Stephen Lam, Dmitry Guschin, Lexi Kopan, Jennifer M. Cherone, Hoang Oanh B. Nguyen, Guijuan Qiao, Yasaman Ataei, Matthew C. MendelRainier Amora, Richard Surosky, Josee Laganiere, B. Joseph Vu, Anand Narayanan, Yalda Sedaghat, Karsten Tillack, Christina Thiede, Annette Gärtner, Seung Kwak, Jonathan Bard, Ladislav Mrzljak, Larry Park, Taneli Heikkinen, Kimmo K. Lehtimäki, Marie M. Svedberg, Jenny Häggkvist, Lenke Tari, Miklós Tóth, Andrea Varrone, Christer Halldin, Andrea E. Kudwa, Sylvie Ramboz, Michelle Day, Jyothisri Kondapalli, D. James Surmeier, Fyodor D. Urnov, Philip D. Gregory, Edward J. Rebar, Ignacio Muñoz-Sanjuán, H. Steve Zhang

*Corresponding author for this work

Research output: Contribution to journal › Article › peer-review

38 Scopus citations

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