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Protein repair: Cusp of a new era in cystic fibrosis
Julia Espel,
Manu Jain
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Corresponding author for this work
Medicine, Pulmonary Division
Research output
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Contribution to journal
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Article
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peer-review
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Keyphrases
Cystic Fibrosis
100%
Cusp
100%
Protein Repair
100%
Cystic Fibrosis Transmembrane Conductance Regulator
83%
Ivacaftor
50%
Clinical Outcomes
16%
Forced Expiratory Volume in 1 Second (FEV1)
16%
Specific Mechanisms
16%
Drug Target
16%
Recent Advances
16%
Functional Class
16%
Genetic Disease
16%
Protein S Deficiency
16%
Approved Indication
16%
Medicine and Dentistry
Cystic Fibrosis
100%
Cystic Fibrosis Transmembrane Conductance Regulator
100%
Ivacaftor
60%
Regulator Protein
40%
Diseases
20%
Genetic Disorder
20%
Forced Expiratory Volume
20%
Patient with Cystic Fibrosis
20%
Regulator Gene
20%
Protein Defect
20%
Drug Delivery System
20%
Pharmacology, Toxicology and Pharmaceutical Science
Cystic Fibrosis
100%
Cystic Fibrosis Transmembrane Conductance Regulator
83%
Ivacaftor
50%
Regulator Protein
33%
Drug Delivery System
16%
Genetic Disorder
16%
Protein Defect
16%
Disease
16%