Safety, tolerability, and pharmacokinetics of casimersen in patients with Duchenne muscular dystrophy amenable to exon 45 skipping: A randomized, double-blind, placebo-controlled, dose-titration trial

Kathryn R. Wagner, Nancy L. Kuntz, Erica Koenig, Lilly East, Sameer Upadhyay, Baoguang Han, Perry B. Shieh*

*Corresponding author for this work

Research output: Contribution to journal › Article › peer-review

14 Scopus citations

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Medicine & Life Sciences